A#L06 #ACR23 @RheumNow
Refractory juv SSc 6m-2y after autolog Stem Cell Tx - 5 patients
HAQ VAS improved 75% (48-99%)
All: mRSS MCID by 6 mo, 87% aver improvement, sustained at 2y
GI: GIT mean 55% improvement, 1 unchanged
FVC stable, DLCO improv >10% in 2, 5-10% in 2
#ACRBest https://t.co/cc6YToVEO5
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14-11-2023


